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5'-Modifications improve potency and efficacy of DNA donors for precision genome editing.
Academic Article
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AAV5 delivery of CRISPR-Cas9 supports effective genome editing in mouse lung airway.
Academic Article
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All-in-one adeno-associated virus delivery and genome editing by Neisseria meningitidis Cas9 in vivo.
Academic Article
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Alpha-1 Antitrypsin Deficiency as a Candidate for Gene Editing.
Academic Article
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Anti-CRISPR AcrIIA5 Potently Inhibits All Cas9 Homologs Used for Genome Editing.
Academic Article
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CRISPR Keeps Things Fresh: Next-Generation Tools for Gene Editing.
Academic Article
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CRISPR-Based Therapeutic Genome Editing: Strategies and In Vivo Delivery by AAV Vectors.
Academic Article
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CRISPR/Cas-Dependent and Nuclease-Free In Vivo Therapeutic Gene Editing.
Academic Article
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CRISPR/Cas9-mediated genome editing induces exon skipping by alternative splicing or exon deletion.
Academic Article
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Debate on Germline Gene Editing.
Academic Article
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Development of Humanized Mice in the Age of Genome Editing.
Academic Article
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Direct Cytosolic Delivery of CRISPR/Cas9-Ribonucleoprotein for Efficient Gene Editing.
Academic Article
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Editorial commentary: A careful approach to gene editing.
Academic Article
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Finding a Treatment for ALS - Will Gene Editing Cut It?
Academic Article
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Genome editing of HBG1 and HBG2 to induce fetal hemoglobin.
Academic Article
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