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Gray-Edwards, Heather

One or more keywords matched the following items that are connected to Gray-Edwards, Heather

Item Type	Name
Concept	Genetic Therapy
Academic Article	Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector.
Academic Article	In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy.
Academic Article	Adeno-Associated Virus Gene Therapy in a Sheep Model of Tay-Sachs Disease.
Academic Article	Lipidomic Evaluation of Feline Neurologic Disease after AAV Gene Therapy.
Academic Article	AAV-mediated gene delivery attenuates neuroinflammation in feline Sandhoff disease.
Academic Article	Biomarkers for disease progression and AAV therapeutic efficacy in feline Sandhoff disease.
Academic Article	Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model.
Academic Article	Mucopolysaccharidosis-like phenotype in feline Sandhoff disease and partial correction after AAV gene therapy.
Academic Article	AAV-mediated gene delivery in a feline model of Sandhoff disease corrects lysosomal storage in the central nervous system.
Academic Article	Sustained normalization of neurological disease after intracranial gene therapy in a feline model.
Academic Article	Therapeutic response in feline sandhoff disease despite immunity to intracranial gene therapy.
Academic Article	Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease.
Academic Article	A Safe and Reliable Technique for CNS Delivery of AAV Vectors in the Cisterna Magna.
Academic Article	7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy.
Academic Article	Volume and Infusion Rate Dynamics of Intraparenchymal Central Nervous System Infusion in a Large Animal Model.
Academic Article	Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice.
Academic Article	Abnormal epiphyseal development in a feline model of Sandhoff disease.
Academic Article	Therapeutic benefit after intracranial gene therapy delivered during the symptomatic stage in a feline model of Sandhoff disease.
Academic Article	Intravenous delivery of adeno-associated viral gene therapy in feline GM1 gangliosidosis.
Academic Article	Real-time MR tracking of AAV gene therapy with ?gal-responsive MR probe in a murine model of GM1-gangliosidosis.
Academic Article	Comparative route of administration studies using therapeutic siRNAs show widespread gene modulation in Dorset sheep.
Academic Article	AAV gene therapy for Tay-Sachs disease.
Academic Article	Redosing Adeno-Associated Virus Gene Therapy to the Central Nervous System.
Academic Article	A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis.
Academic Article	Life-Limiting Peripheral Organ Dysfunction in Feline Sandhoff Disease Emerges after Effective CNS Gene Therapy.
Academic Article	Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation.
Academic Article	A minimally invasive endovascular approach to the cerebellopontine angle cistern enables broad CNS biodistribution of scAAV9-CB-GFP.
Academic Article	Neuroimaging Applications for the Delivery and Monitoring of Gene Therapy for Central Nervous System Diseases.
Academic Article	Intravenous gene therapy improves lifespan and clinical outcomes in feline Sandhoff Disease.

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Gene therapy