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Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy. Reply.

Lek A, Keeler A, Flotte TR. Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy. Reply. N Engl J Med. 2023 Dec 07; 389(23):2211.

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