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[Gene therapy in lysosomal diseases].
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[Gene therapy in lysosomal diseases].
Moullier P, Salvetti A, Bohl D, Danos O, Heard JM. [Gene therapy in lysosomal diseases]. C R Seances Soc Biol Fil. 1996; 190(1):45-51.
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subject areas
Animals
Cats
Dogs
Fibroblasts
Gene Transfer Techniques
Genetic Therapy
Humans
Iduronidase
Lysosomal Storage Diseases
Mice
Mucopolysaccharidosis I
Rats
Replantation