Sustained efficacy of CRISPR-Cas13b gene therapy for FSHD is challenged by immune response to Cas13b.
Rashnonejad A, Farea M, Amini-Chermahini G, Coulis G, Taylor N, Fowler A, Villalta A, King OD, Harper SQ. Sustained efficacy of CRISPR-Cas13b gene therapy for FSHD is challenged by immune response to Cas13b. bioRxiv. 2024 Dec 19.