Header Logo

In vivo gene editing works in humans: Results of a phase 1 clinical trial for TTR amyloidosis.

Batista AR, Flotte TR. In vivo gene editing works in humans: Results of a phase 1 clinical trial for TTR amyloidosis. Mol Ther. 2021 09 01; 29(9):2633-2634.

View in: PubMed