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Improving preoperative identification of infants at risk for severe retinopathy of prematurity.
Oligohymenophorea
Ureteral Neoplasms
Virgibacillus
Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency.
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Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency.
Gruntman AM, Flotte TR. Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency. Methods Mol Biol. 2017; 1639:267-275.
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PubMed
subject areas
alpha 1-Antitrypsin
alpha 1-Antitrypsin Deficiency
Gene Editing
Genetic Therapy
Humans
Liver Diseases
Lung Diseases
authors with profiles
Alisha M Gruntman DVM, PhD
Terence R Flotte MD