Recombinant adeno-associated virus vectors for gene therapy.
Conlon TJ, Flotte TR. Recombinant adeno-associated virus vectors for gene therapy. Expert Opin Biol Ther. 2004 Jul; 4(7):1093-101.
-
Animals
-
Biological Transport
-
Capsid
-
Clinical Trials as Topic
-
Dependovirus
-
DNA, Recombinant
-
DNA, Single-Stranded
-
DNA, Viral
-
Gene Expression Regulation, Viral
-
Genes, Synthetic
-
Genetic Therapy
-
Genetic Vectors
-
Humans
-
Injections, Intramuscular
-
Muscle Fibers, Skeletal
-
Mutagenesis, Insertional
-
Receptors, Virus
-
Transduction, Genetic