Below are the most recent publications written about "Genetic Vectors" by people in Profiles.
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Maguire AS, Ta NL, Gross AL, Garrett CJ, Zimmerman AD, Diffie EB, Osterhoudt DE, Pacer SH, Mitchell ML, Cannon JS, Hall PI, Sandey M, Cole RC, Seyfried TN, Gray-Edwards HL, Sena-Esteves M, Martin DR. Intravenous gene therapy improves life span and clinical outcomes in a feline model of Sandhoff disease. Sci Transl Med. 2026 09 09; 18(866):eadx2447.
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Rosen BC, Mauter JT, Voigt TB, de Figueiredo Godoy G, Walker EL, Louw JJ, Ghosh N, Panayiotou C, Yrizarry-Medina A, Terao J, Rakasz EG, Reynolds MR, Dudley DM, Reed DS, Watkins DI, Ricciardi MJ. Elicitation of Potent H5N1- and H7N9-Neutralizing Antibody Responses in Rhesus Macaques by Sequential Heterologous Vaccination with mRNA and Adenoviral Vectors Encoding Full-Length Hemagglutinins. Viruses. 2026 09 07; 18(9).
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Batista AR, Scholand AC, Callahan WS, Watson MK, Sion CM, Mola T, O'Hara K, Wentworth SA, Sena-Esteves WS, King OD, King RM, Sena-Esteves M. AAV-mediated gene therapy demonstrates phenotypic rescue in a mouse model of Cockayne syndrome. J Clin Invest. 2026 09 15; 136(18).
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Messias SGDS, de Paula IÉS, Cardoso KF, Garcia CC, de Mendonça Ângelo ALP, de Faria Gonçalves AP, Melo EM, Tavares LP, Faustino LP, Alves PA, Dos Reis JGAC, Teixeira-Carvalho A, Antonelli LRDV, Xavier MAP, Martins-Filho OA, Machado AMV, Araújo MSS. Assessment of a recombinant influenza virus carrying interleukin 7 gene as a platform for novel immunotherapeutic approaches. Immunol Lett. 2026 Dec; 282:107223.
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Wan F, He J, Ma H, PiresFerreira D, Kumanan V, Lee JS, Chen X, He R, Su Q, Gallagher TL, Zhu S, Cabrera GT, Zhao L, Shen J, Gruntman A, Brown RH, Xu Z, Gao G, Xie J. Intravenous administration of an engineered AAV9-gene-silencing vector suppresses human SOD1 and extends survival in an ALS mouse model. Nat Commun. 2026 06 25; 17(1).
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Story BD, Thomasy SM, Adelman SA, Taghian T, Lopez Y, Ardon M, Shiraishi H, Khan S, Khan M, Do M, Benatti HR, Bertrand S, Prestigiacomo R, Gately R, Martin DR, Sena-Esteves M, Xie J, Gao G, Teixeira LBC, Shaw GC, Marsh-Armstrong N, Gray-Edwards HL. Cerebrospinal delivery of a bidirectional AAV9 vector improves optic nerve and retinal pathology in a sheep model of Tay-Sachs disease. Mol Ther. 2026 Sep 02; 34(9):5498-5509.
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Khanduja S, Raman V, Hall CL, Howell LM, Van Dessel N, Forbes NS. Salmonella vector creates de novo parvovirus that reduces solid tumors and forms antitumor immune memory. Cell Rep Med. 2026 Jun 16; 7(6):102839.
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Chen X, Xie Q, Nath SJ, Tang M, Ma H, Günes YÖ, Sharma T, Liu H, Cui M, Du A, Lu M, Liu SY, Wassamon B, Xu M, Wu JY, Su Q, Fitzgibbons TP, Liu J, Wan F, Kumanan V, He R, Ma Y, Yang J, Gray-Edwards HL, Gallagher TL, Tai PWL, Gao G, Xie J. Long-term comparative analysis of AAV9-mediated gene replacement therapies for spinal muscular atrophy in mice. Nat Commun. 2026 May 23; 17(1).
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Tang Q, Pires-Ferreira D, Mueller C, Gruntman AM, Flotte TR. Optimization of Alpha-1 Antitrypsin Expression from Adeno-Associated Virus Vectors. Hum Gene Ther. 2026 Jul; 37(13-14):609-617.
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Wang J, Turgeon CT, Loken PR, Gray-Edwards H, Gao G, Tortorelli S, Wang D, Strauss KA. Systemic dual-gene therapy reverses biochemical intoxication in the central metabolic compartment of Bckdha-/- mice. Mol Ther. 2026 Aug 05; 34(8):4569-4580.